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Solid Biosciences has been granted Orphan designation by the European Commission for SGT-212, its investigational gene therapy targeting Friedreich’s ataxia.
The company also announced that five patients have now been dosed in its Phase 1b FALCON clinical trial. These developments mark key steps in the advancement of Solid Biosciences programs addressing rare neuromuscular disorders.
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Solid Biosciences recently launched POLARIS-101, a next-generation muscle-tropic capsid designed to improve gene therapy delivery for neuromuscular and cardiac conditions. The company is also scheduled to present seven posters on Duchenne therapies and platform technologies at ESGCT2026, according to a previous announcement regarding its upcoming presentations. These initiatives reflect Solid Biosciences' continued focus on advancing gene therapies for rare diseases.